| NFND | National Foundation for Neuromuscular Diseases |
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| NIADDK | National Institute of Arthritis, Diabetes, Digestive and Kidney Diseases |
| NIAID | National Institute of Allergy and Infectious Diseases |
| NIAMDD | National Institute of Arthritis, Metabolism, and Digestive Diseases |
| NIAMS | National Institute of Arthritis, Musculoskeletal and Skin Diseases |
| lysosomal storage diseases | Inborn errors of metabolism characterised by defects in specific lysosomal hydrolases and resulting in intracellular accumulation of unmetabolised substrates. (12 Dec 1998) |
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